health smarts. Synthetic Promise

February 2012
PN;Feb2012, Vol. 66 Issue 2, p22
Trade Publication
The article reports on the result of the study conducted by the researchers at the University of Missouri which reveals that targeting a synthetic molecule to a specific gene could lower the severity of the disease spinal muscular atrophy (SMA). According to researcher Chris Lorson, the mice which received synthetic RNA gain more weight, live longer, and show improvements in motor skills. It notes that SMA is considered the leading genetic cause of infantile mortality in the world.


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