July 2010
Worldwide Biotech;Jul2010, Vol. 22 Issue 7, p1
Trade Publication
The article deals with the results reported by Celladon Corp. in July 2010 from its Phase 2 clinical trial of Mydicar, a genetically targeted enzyme replacement therapy. Accordingly, the findings demonstrated the primary safety and efficacy endpoints for high dose Mydicar against placebo. Noted benefits in patients included significant reduction in cardiovascular events and improved exercise tolerance and cardiac function. Other details of the Calcium Up-regulation by Percutaneous administration of gene therapy in cardiac disease (CUPID) trial are cited.


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