Neurodevelopmental Outcomes of Children with Infantile Krabbe Disease Treated with Umbilical Cord Blood Transplantation: 10 Years of Follow-up

Escolar, Maria L.; Yelin, Karina; Poe, Michele D.
December 2006
Current Medical Literature: Lysosomal Storage Disease;2006, Vol. 6 Issue 3, p65
Academic Journal
The article focuses on a study conducted in order to determine the neurodevelopmental outcomes of children infected with infantile Krabbe disease, who were treated with umbilical cord blood transplantation. It has been discovered that neurodevelopment in 90% of patients continued at an age-appropriate rate in cognitive behavior, receptive language and fine motor skills. 23% of patients continued to use augmentative communication due to difficulties with articulating words.


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