TITLE

CSCI/RCPSC Henry Friesen Lecture: Cell therapy for Duchenne Muscular Dystrophy

AUTHOR(S)
Tremblay, Jaques P.
PUB. DATE
December 2006
SOURCE
Clinical & Investigative Medicine;Dec2006, Vol. 29 Issue 6, p378
SOURCE TYPE
Academic Journal
DOC. TYPE
Article
ABSTRACT
The article focuses on the cell therapy for Duchenne muscular dystrophy (DMD). DMD, which is a fatal hereditary disease, is caused by an X-linked genetic defect resulting to absence of dystrophin. Among the approaches for treating DMD is gene therapy, which aims to direct dystrophin gene in the patient's muscle therapy. Key information regarding the clinical trial of cell therapy are further discussed.
ACCESSION #
23637432

 

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