The Path of Discovery in Understanding the Biology of Cystic Fibrosis and Approaches to Therapy

Welsh, Michael J.
August 1994
American Journal of Gastroenterology;Aug1994 Supplement, Vol. 89 Issue 8, pS97
Academic Journal
Discusses the path of discovery in understanding the biology of cystic fibrosis (CF) and approaches to therapy. Description of the physiological defect in CF epithelia; Identification of gene and mutations that encodes CF transmembrane conductance regulator; Discussion on how mutations case dysfunction of the gene product.


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