Gene therapy: two steps forward, one step back

Johnston, Josephine; Baylis, Francoise
June 2004
CMAJ: Canadian Medical Association Journal;6/8/2004, Vol. 170 Issue 12, p1785
Academic Journal
Focuses on the gene therapy trial involving children with X-linked sever combined immunodeficiency disease (X-SCID) which began in 1999 in Paris, France. Setback to the Paris trial; Reaction of the international community in the first case of leukemia in the Paris trial; Harm-benefit analysis of gene therapy trial.


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